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Neurology

Duchenne Muscular Dystrophy Clinic

UR Medicine / Neurology / Our Divisions / Neuromuscular Disease Center / Multidisciplinary Clinics / Duchenne Muscular Dystrophy Clinic / Research and Clinical Trials

If you are interested in receiving information about clinical trials available for Duchenne Muscular Dystrophy please email Dr. Ciafaloni.

Current Clinical Trials

FOR-DMD

 

  1. FOR-DMD: Double-blind randomized trial to optimize steroid regimen in Duchenne MD (1 R01 NS061799-01A2)
  2. An Open-Label, Multi-Center Study to Evaluate the Safety and Tolerability of Eteplirsen in Patients with Advanced Stage Duchenne Muscular Dystrophy (Sarepta)
  3. An Open-Label, Multi-Center, 48-Week Study with a Concurrent Untreated Control Arm to Evaluate the Efficacy and Safety of Eteplirsen in Duchenne Muscular Dystrophy (Sarepta)
  4. A Pharmacokinetic Study of Oral Deflazacort in Children and Adolescent Subjects With Duchenne Muscular Dystrophy (Marathon Pharmaceuticals, LLC)
  5. An Open-Label, Long-Term Extension Study to Evaluate the Safety and Tolerability of Deflazacort in Duchenne Muscular Dystrophy (Marathon Pharmaceuticals, LLC)